Nusinersen, marketed as Spinraza, is a medication used in treating spinal muscular atrophy (SMA), a rare neuromuscular disorder. In December 2016, it became the first approved drug used in treating this disorder.
via Wikipedia infobox
Nusinersen, marketed as Spinraza, is a medication used in treating spinal muscular atrophy (SMA), a rare neuromuscular disorder. In December 2016, it became the first approved drug used in treating this disorder.
Since the condition it treats is so rare, nusinersen has so-called "orphan drug" designation in the United States and the European Union.
Discovered by embedding cosine similarity (sentence-transformers MiniLM, 384-dim).