Risdiplam, sold under the brand name Evrysdi, is a medication used to treat spinal muscular atrophy (SMA) and is the first oral medication approved to treat this disease by the US Food and Drug Administration (FDA).
via Wikipedia infobox
Risdiplam, sold under the brand name Evrysdi, is a medication used to treat spinal muscular atrophy (SMA) and is the first oral medication approved to treat this disease by the US Food and Drug Administration (FDA).
Risdiplam is a survival of motor neuron 2-directed RNA splicing modifier.
Discovered by embedding cosine similarity (sentence-transformers MiniLM, 384-dim).